A Study Comparing Two Doses of AGTC-501 in Male Subjects With X-linked Retinitis Pigmentosa Caused by RPGR Mutations (SKYLINE)

Authors
Category Primary study
Registry of Trialsclinicaltrials.gov
Year 2021
This study will evaluate the safety and efficacy of a recombinant adeno-associated virus vector (rAAV2tYF-GRK1-RPGR) in patients with X-linked retinitis pigmentosa caused by RPGR mutations.
Epistemonikos ID: fc5ff4e1f342248a90ba0fe35a169b22e766da30
First added on: May 15, 2024