GDNF Gene Therapy for Multiple System Atrophy

Authors
Category Primary study
Registry of Trialsclinicaltrials.gov
Year 2023
The objective of this randomized, double-blinded, placebo-controlled Phase 1 investigation is to evaluate the safety and potential clinical effect of AAV2-GDNF delivered to the putamen in subjects with either a possible or probable diagnosis of Multiple System Atrophy.
Epistemonikos ID: f8889b26fee9fd61124e386c3c146cf3eb7a1d91
First added on: May 08, 2024