Design of a Phase 1/2 Open-Label, Dose-Escalation Study of the Safety and Efficacy of Gene Therapy in Adults With Classic Congenital Adrenal Hyperplasia (CAH) Due to 21-hydroxylase Deficiency Through Administration of an Adeno-Associated Virus (AAV) Serotype 5-Based Recombinant Vector Encoding the Human CYP21A2 Gene

Category Primary study
JournalJournal of the Endocrine Society
Year 2021
This article has no abstract
Epistemonikos ID: c3415a6132626a4a0c5376dbbbbeef572625eb91
First added on: Jun 13, 2024