Relevance of NHP safety studies for ocular delivery of AAV-based gene therapy in humans: Example of gs010 (raav2/2-nd4) local tolerability, shedding and immunogenicity for the treatment of leber hereditary optic neuropathy (LHON), after intravitreal (IVT) injection in non-human primates (NHP) and in LHON patients

Category Primary study
JournalInvestigative Ophthalmology and Visual Science
Year 2015
This article has no abstract
Epistemonikos ID: be402aff208438ecbd63fb081f1e5733149ef879
First added on: Feb 08, 2025