A Phase I/II Safety, Tolerability, Ascending Dose and Dose Frequency Study of Recombinant Human Heparan-N-sulfatase (rhHNS) Intrathecal Administration via an Intrathecal Drug Delivery Device in Patients With Sanfilippo Syndrome Type A (MPS IIIA)

Authors
Category Primary study
Registry of TrialsOverview of Medical Research in the Netherlands
Year 2010
This article has no abstract
Epistemonikos ID: 9e9e78d537d1f05cff65d0a421a97c3b819f8bd6
First added on: Apr 16, 2025