SMA – THERAPY: P.261 Long-term follow-up of onasemnogene abeparvovec gene therapy in spinal muscular atrophy type 1 (SMA1)

Category Primary study
JournalNeuromuscular Disorders
Year 2020
This article has no abstract
Epistemonikos ID: 7e92264133b11255d1ca71d93ca0992474853a48
First added on: Feb 12, 2025