EFFICACY AND SAFETY OF THE RECOMMENDED PEGVALIASE DOSING REGIMEN IN ADULTS WITH PHENYLKETONURIA IN THE PHASE 3 PRISM STUDIES

Authors
Category Primary study
JournalMolecular Genetics and Metabolism
Year 2022
This article has no abstract
Epistemonikos ID: 6c8b93fde7ccc63d13faa82dc9328d2a6699a15e
First added on: Feb 14, 2025