An open-label, single-arm, multicenter study of intracerebral administration of adeno-associated viral vectors serotype rh.10 carrying the human N-sulfoglycosamine sulfohydrolase (SGSH) cDNA for the treatment of mucopolysaccharidosis type IIIA (MPS IIIA)

Authors
Category Primary study
Registry of TrialsOverview of Medical Research in the Netherlands
Year 2018
This article has no abstract
Epistemonikos ID: 5b669f447e3e5962e63dee3fba1bfdc9e2472d72
First added on: Apr 11, 2025