First drug registry in Duchenne muscular dystrophy (DMD) to assess Translarna (Ataluren) use, safety, and effectiveness in routine clinical practice

Category Primary study
JournalNeuromuscular Disorders
Year 2015
This article has no abstract
Epistemonikos ID: 56b342522c2e424c803f403fc4deb42b72e35f84
First added on: Feb 07, 2025