AUTOPHAGIC MYOPATHIES / MYOFIBRILLAR MYOPATHIES / DISTAL MYOPATHIES / POMPE DISEASE: P.03 NEO1/NEO-EXT studies: Safety and exploratory efficacy of repeat avalglucosidase alfa dosing after up to 6 years in late-onset Pompe disease (LOPD)

Authors
Category Primary study
JournalNeuromuscular Disorders
Year 2020
This article has no abstract
Epistemonikos ID: 494d9057d4fd6d34a5cb5df5329a433764f1b2fc
First added on: Feb 12, 2025