A Study to Determine the Efficacy and Safety of Luspatercept in Adult Participants and to Evaluate the Safety and Pharmacokinetics in and Adolescent Participants With Alpha (α)-Thalassemia

Authors
Category Primary study
Registry of TrialsClinicalTrials.gov
Year 2022
The purpose of the study is to evaluate the efficacy and safety of luspatercept plus bestsupportive care (BSC) vs placebo plus BSC on anemia in adult participants withα‐thalassemia hemoglobin H (HbH) disease and determine the safety and drug levels inadolescent participants.
Epistemonikos ID: 421ffeb4aa9bd48dbd77a2c46a802744faa3d057
First added on: May 14, 2024