A Phase 3 Open-Label Study of PTC923 (Sepiapterin) in Phenylketonuria

Authors
Category Primary study
Registry of TrialsClinical Trials Information System
Year 2025
This article has no abstract
Epistemonikos ID: 2436d61368e6e93cda64798b7246d5416d8daa08
First added on: Jan 16, 2026