Safety and Efficacy of Clenbuterol in Individuals With Late-onset Pompe Disease and Receiving Enzyme Replacement Therapy

Authors
Category Primary study
Registry of Trialsclinicaltrials.gov
Year 2013
Funding Source- FDA OOPD The purpose of this study is to investigate the safety and efficacy of clenbuterol on motor function in individuals with late-onset Pompe disease (LOPD) who are treated with enzyme replacement therapy (ERT).
Epistemonikos ID: 22ce0b0406ebebab2c2591394b7d6e4006a343f3
First added on: May 11, 2024