An Open-Label, Single-Arm, Multicenter Study of Intracerebral Administration of Adeno-Associated Viral Vectors Serotype rh10 Carrying the Human N-sulfoglucosamine sulfohydrolase (SGSH) cDNA for the Treatment of Mucopolysaccharidosis Type IIIA

Authors
Category Primary study
Registry of TrialsEU Clinical Trials Register
Year 2018
This article has no abstract
Epistemonikos ID: 1d15683e5aeac770a4490df2d37a87df35f34789
First added on: Apr 17, 2025