A Registry of Cases of Spinal Muscular Atrophy

Authors
Category Primary study
Registry of TrialsClinicalTrials.gov
Year 2026
Because no long-term record of prenatal Spinal Muscular Atrophy (SMA) treatment exists, this study will address an important gap in the understanding of the safety and benefit of treatment while in the womb. The registry will help guide best practices for monitoring pregnant women and their fetus with SMA, if treated with a medication while in the womb, and to follow the baby after birth for signs of safety and added benefit birth and support future research and study development.
Epistemonikos ID: 1b51707f450166420d68d0cb3a012585a606cb31
First added on: Sep 05, 2026